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Demonstrated ability to induce patient-derived Fanconi Anemia cells to pluripotency for patient-specific therapeutic cell derivation.
Demonstrates efficient reprogramming of human cells on nanofibrous polymeric substrates.
DNA methylation of Runx1 regulatory regions correlates with transition from primitive to definitive hematopoietic potential in vitro and in vivo.September 12, 2013
Examines the role DNA methylation of regulatory elements plays in the performance of the Runx1 promoter switch during hematopoietic stem cell (HSC) development.
Examined efficacy of TALEN technology to correct gene mutations and provided a safety profile for translational application of TALEN gene-editing.
Hematopoietic differentiation of induced pluripotent stem cells from patients with mucopolysaccharidosis type I (Hurler syndrome).January 1, 2011
Describes use of induced pluripotent stem cells in the treatment and disease modeling of Hurler syndrome.